Title | Splice-correcting oligonucleotides restore BTK function in X-linked agammaglobulinemia model |
Publication Type | Journal Article |
| 2014 |
Authors | Bestas, B, Moreno, PMD, Blomberg, KEM, Mohammad, DK, Saleh, AF, Sutlu, T, Nordin, JZ, Guterstam, P, Gustafsson, MO, Kharazi, S, Piatosa, B, Roberts, TC, Behlke, MA, Wood, MJA, Gait, MJ, Lundin, KE, El Andaloussi, S, Mansson, R, Berglof, A, Wengel, J, Smith, CIE |
Journal | Journal of Clinical Investigation |
Volume | 124 |
Pagination | 4067-4081 |
Date Published | 2014 |
| 0021-9738 |
| <Go to ISI>://WOS:000341168100038 |